Topics

Meveol®
Hello I have just read: « A new treatment against cystic fibrosis could emerge by 2016. This is a project supported by Bpifrance (bank financing and investment) who just released € 10 million for a new medical program called Alipex. Of the three companies involved in research: Alaxia, a ...
15.04.2014
Living in Athens with CF Recommended ?
I have an 11 year old daughter with CF and we live in Abu Dhabi, UAE, but we may come to live in Athens, I am worried about the air pollution, we will be living in the hills outside Athens. Also Gala has just started to take Ivacaftor as she has the G551 mutation, is this going to be available ...
24.03.2014
Kalydeco® off-label
Dear expert team, my son has the following CFTR mutations: 1717-1G>A (class 1) und die mutation S549R (gating/connection, class 2 oder 3) Kaleydeco ® has indeed at the moment only market authorization for the class 3 mutation G551D. However, tests with other mutations have been done. There it ...
12.02.2014
MIGLUSTAT
Hello Do you have any news regarding research about MIGLUSTAT? Thank you.
03.02.2014
Therapy of the protein
Hello, We have learned in September by the "INSERM" (french national institute for health and medical research), about the discovery of 2 molecules acting on deltaF508 CFTR protein. What is the difference between theses 2 molecules and Vertex’s molecules (Ivacaftor® and Lumacaftor®) that are ...
08.01.2014
POTENTIATOR / GALAPAGOS
Hello An article published on 12/16/13 indicates that the biotechnology company Galapagos has a new drug candidate (potentiator) which will be tested in clinical trials. How much credit can you give to this notification? Have you more information? Thanks
08.01.2014
Delta F 508
Thank you in advance for giving us the latest positive or negative but true results on combined VX 770 and VX 809 clinical trials for example as we read everything and its opposite. It would be good to have regular news because for us, sick or close to sick people with CF, it is the little light ...
01.01.2014
CF cure
Where do we start to cure CF?
23.12.2013
508 r117h T5
My grandson has recently been diagnosed with CF. His details are 508 and r117h T5. Sweat test 47. What CF symptoms will develop? Also - what medication will be available in the near future which may address the symptoms? Thank You
02.12.2013
State of research?
Dear expert team, How far advanced is the current state of research on VX809 really? Is there a chance for this drug to be released to the market this year (2013)? And is it correct that it is only applicable to the Delta F508 homozygous mutation – and only to patients in very bad ...
04.11.2013
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