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Delta F508 effective 2015
- Question
- Hello,
my 12-year-old daughter suffers from the above mentioned mutation. I have heard, that there is a drug available in the course of this year. Is it true and how does it act?
Thank you - Answer
- Dear questioner,
drugs for the treatment of the mutation F508del-CFTR are until now not available on a prescription from the physician - the known potentiators and correctors of the company Vertex are at the moment still investigated in the frame of clinical studies
Please follow this link for further information [in German]:
muko.info/forschung/news-detail-und-archiv/detailansicht/article/ergebnisse-der-vertex-studien-mit-der-kombination-von-lumacaftor-und-ivacaftor-bei-f508del-homozyg/17.html
Best regards,
Frauke Stanke - 04.06.2015
