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Replace a gene with a special method
- Question
- Hello, is the CRISPR / cas9 method envisaged in cystic fibrosis?
Are trials going on?
Thank you - Answer
- Hello
CRISPR/cas9 is a tool to intervene very specifically on genetic material.
It is already used in the context of cystic fibrosis in basic research, eg for the development of models such as organoids ( "new structure resembling an organ" - the organoid is used in medicine and to test new biological functions, new molecules or to recreate and visualize, in an integrated system, the activity of an existing organ).
We will certainly hear about it in the coming years. This tool is not yet used in clinical trials.
Paola De Carli
Research Department Director
French CF Association "Vaincre La Mucoviscidose" - 08.04.2016
