Topics

Treated with Kalydeco®. And then?
Hello, patients receiving a treatment like Kalydeco®, do they have a different life? I mean by that, do they still need to take many drugs such as Creon®, do they still do a lot of physiotherapy? Or it is case by case? Is there an increase in life expectancy, but is their life a little more ...
15.09.2014
Vertex - results of a phase 2 study for patients heterozygous for F508del
Hello The Vertex company has published results regarding patients heterozygous for the F508del mutation, here is the link: http://investors.vrtx.com/releasedetail.cfm?releaseid=862727. It seems to me that patients heterozygous for the F508del mutation could have a potential treatment like the one ...
15.09.2014
F508del mutation treatment
Hello, following the results released yesterday by Vertex to treat patients with two delta F508 mutations, what it about the patients with only one delta F508 mutation? In fact, when our son was born in 2011 we were told that there will be a cure for one of the two mutations, but for now I can ...
10.09.2014
Ivacaftor-lumacaftor combination in F508del homozygous patients
Could you give us some details for the double deltaF508 mutation? Is the Ivacaftor - lumacaftor combination study positive and in that case, how long will it take until market authorization for those drug and to treat a large proportion of sick patients. Thank you in advance for your response.
10.09.2014
Ivacaftor and Lumacaftor
The results of the phase 3 study have been published a few days ago. There were slight improvements in the 24-weeks study. How can I judge the resutls realistically for the future (timely manner, in case of long-term intake change of the mean life expectancy)? Many thanks for your time
21.08.2014
Colloidal silver
Can colloidal silver be taken for fighting bacteria in case of CF and can it also be inhaled? Is there any recent research?
21.08.2014
Kalydeco® and body height
Dear expert team, I have already wrote to you once concerning the off-label use of Kalydeco® with my son Till. He is taking now Kalydeco® for 10 weeks. He is 8-years old and has the mutation 1717 1G>A and the gating mutation S549R. Kalydeco® has a very good effect in him without negative side ...
18.08.2014
Last results of the phase 3 cinical trial VX661 and ivacaftor
Hello could you inform us regarding results of the clinical phase 3 which has just ended with patients homozygous for the F508del mutation and performed by the Vertex company. Thank you
29.07.2014
Phage therapy
Ten years ago I have already sent a question to Vaincre la mucoviscidose (French CF patient organization) concerning the subject without a really satisfactory answer. While antibiotic resistance is becoming a social problem why isn't the use of phage therapy further developed, even if the results ...
29.07.2014
Vaccine against Pseudomonas aeruginosa
Hello There was a clinical trial for Pseudomonas vaccine. What are the news about this clinical trial? Are results available? Thank you.
29.07.2014
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