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Effect of Trikafta
Dear experts, our son is 1 year old and has the mutations del508 and W1218X. We have a question on the effect of modulator therapy. He will get Kaftrio (Trikafta) due to his one del508 mutation. Is there any knowledge about the effect of Kaftrio (Trikafta) in case of this mutation combination? We ...
07.11.2023