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Keywords
- ABPA_Aspergillus
- accompanying diseases
- air-improving devices
- allergy
- animals_pets
- antibiotic therapy
- asthma
- complementary medicine
- covid-19
- diabetes
- diagnostics
- drugs side effects
- drugs under development_genetic therapy
- ENT
- general aspects
- genetics
- health care
- hepatobiliary disease
- hygiene
- i.v.-lines
- inhalation
- lung
- microbiology
- miscellaneous
- modulator therapy
- MRSA
- nutrition and GI problems
- oxygen supplementation_therapy
- physiotherapy
- Pseudomonas aeruginosa
- psychosocial
- public facilities
- recreational activities
- reproduction
- research
- social law
- sport
- swine flu_novel influenza
- transplantation
- travelling
- vaccination
- ventilation
Topics
- Replace a gene with a special method
- Hello, is the CRISPR / cas9 method envisaged in cystic fibrosis? Are trials going on? Thank you
- 08.04.2016
- Mutations F508del & I507del
- Hello, We are the proud parents of a beautiful boy with the mutations F508 and I507. We would like to have more information on both mutations together. Our son’s disease looks more digestive than respiratory, although he already had two pseudomonas colonizations (halted by an oral cure and an ...
- 27.02.2016
- CF Treatments
- Hi, I'm a CF, I am 15 years old. I am looking for new drugs. I'd like your response. Thank you.
- 27.02.2016
- Orkambi® prescription
- Hello My son aged 30, has a F508del mutation but has not been offered ORKAMBI® yet. His FEV1 is 27% and he made all pre-transplant tests a year ago. Are all patients taken into consideration for Orkambi or are there cases where this treatment is not recommended? Has he to request it from the ...
- 27.02.2016
- Orkambi®, temporary authorization for Use
- Hello, A cohort Temporary Authorisation for Use was granted for ORKAMBI® (beginning of ATU: December 2015, ...
- 27.02.2016
- Lynovex (Cysteamine)
- Dear team, while surfing in the Internet, I came across the above mentioned candidate that is acutally in Phase IIb. I was not able to find anything about it on the German CF websites. The pharmaceutical newspaper [German newspaper] reported in January 2015: “The experimental antibacterial ...
- 14.01.2016
- Ataluren® and Bramitob®
- I have CF and the mutations F508del & L732X. I am 29 years old and I take for many years Bramitob® (Tobramycin for inhalation). Can I take Ataluren®?
- 14.12.2015
- Ataluren
- Is the new medication Ataluren appropriate for administration for the mutation G126D?
- 11.12.2015
- Which mutation has more need for therapy?
- Dear expert team, my son (4 years, CF) has the following known mutations: delF508 (inherited by me) and on the other allele R1070Q-S466X. The R1070Q is a missense mutation, the S466X is a nonsense mutation. In case of this rare combination, a marked pancreatic insufficiency has to be expected, ...
- 09.11.2015
- Gene editing
- Hello, The last magazine edited by the French CF patient organization indicates that genetic editing techniques, for correcting the genetic material in a relatively simple and inexpensive way, have been developed. They allow to avoid vectors and correct cells directly. Could we have more ...
- 12.10.2015